New Treatments for Rare Monogenic Neurological Disorders

Thu Jan 10, 2019
Florian Eichler, MD, Is the director of the Leukodystrophy Service at Massachusetts General Hospital. In this video, Dr. Eichler discusses his research focused on rare, single-gene neurological disorders that have a devastating impact on patients’ lives. He highlights his successful gene therapy clinical trial in boys with cerebral adrenoleukodystrophy, where the large majority of these children stabilized over a two-year period.Read more here: in Motion provides health care professionals with information about the latest breakthroughs, research and clinical advances from Massachusetts General Hospital.Subscribe: